The U.S. Food and Drug Administration approved Abeona Therapeutics' gene therapy for a rare skin disorder on Tuesday.

The first patient to receive a new gene therapy at the Children's Hospital of Philadelphia is now living pain-free for the ...

As tariffs, HHS workforce cuts and the ouster of CBER Director Peter Marks threaten the “lifeblood” of the cell and gene ...

Despite reports of a sickle cell patient being cured by gene therapy, columnist Oluwatosin Adesoye explains why she remains ...

A new gene therapy reversed heart failure in pigs by repairing heart function through cBIN1, showing major promise for future ...

Amid a reckoning for the gene therapy field, Vertex Pharmaceuticals has joined a growing list of companies paring back their ...

Many diseases are caused by a missing or defective copy of a single gene. For decades, scientists have been working on gene ...

Fran Gregory, PharmD, MBA, VP of emerging therapies at Cardinal Health, talks about the importance of market access ...

Researchers at the University of Minnesota have completed a first-in-human clinical trial testing a CRISPR/Cas9 gene-editing ...

Abeona Therapeutics' Zevaskyn, a cell therapy based on engineered keratinocytes harvested from patients, has been approved in ...

To help achieve more precise control of gene therapy, engineers have designed a new control circuit that can keep gene expression levels within a target range. The method could be used to deliver ...

The US Food and Drug Administration (FDA) has approved the first cell-based gene therapy for a rare genetic skin disorder.