Even as many countries globally recognise Subacute Sclerosing Panencephalitis (SSPE) as a rare disease, it remains a serious ...

FDA Commissioner Marty Makary’s proposal to roll out a new drug approval pathway is heightening hope for the rare disease ...

“Most rare disease data has been collected from people of European ... Find AP’s standards for working with philanthropies, a ...

In her spare time, Oxana volunteers at the International Rare Disease Research Consortium (IRDiRC), where she is co-chair of the Regulatory Scientific Committee (RSC). In this interview, Oxana ...

Stealth BioTherapeutics had expected the FDA to respond on Tuesday to its marketing application for elamipretide to treat ...