Capricor Therapeutics said on Monday the U.S. Food and Drug Administration (FDA) plans to convene a panel of outside experts ...

From STAT’s Adam Feuerstein: The FDA informed Capricor Therapeutics that a meeting of outside experts will be convened to ...

Parents of a boy with Duchenne Muscular Dystrophy are toasting another boost to their campaign to find a cure, with a new ...

Mail campaign, NHSGGC confirmed eligible kids should be given givinostat before the end of May, however those in other health ...

While right-wing populism surges in some of the world’s leading democracies, Chile’s leftist government is rushing in the ...

In April, the Deparment of Health and Human Services shuttered the committe that oversaw newborn screenings. Advocates hope ...

ABEL Motorsports driver Callum Hedge (photo) is trying to raise awareness and funds to combat muscular dystrophy in his native New Zealand, as two of his nephews suffer from the disorder.

Dyne Therapeutics (DYN) announced that the European Commission has granted orphan drug designation for DYNE-251 for the treatment of Duchenne ...

The antimalarial drug mefloquine could help treat genetic diseases such as cystic fibrosis, Duchenne muscular dystrophy, as well as some cancers.

I really want to drill down on the power of the smile and spend time talking about the last two, Pan Am vs Duchenne, which are the two most talked about and most dissected by social and political ...

This study was funded by the Azrieli Foundation, the National Institutes of Health (NIH), Myotonic Dystrophy Foundation, Muscular Dystrophy Association, the UNVL startup fund, the University of ...