A community has come together to surprise 9-year-old Killian Bauer who is living with Duchenne Muscular Dystrophy, with a ...

A community has come together to surprise 9-year-old Killian Bauer who is living with Duchenne muscular dystrophy, with a ...

While there have been reports from drugmakers about possible interruptions with FDA matters due to staff layoffs, one company ...

She visited Fann hospital in Dakar, where neurologist Dr. Pedro Rodriguez measured her lung capacity. He suspects Mariama had ...

Friday a group of local childhood friends embarked on a journey down the Rogue River, hoping to get to all the way to the ...

The company anticipates submitting a biologics licence application for accelerated approval in the US in early 2026.

ABEL Motorsports driver Callum Hedge (photo) is trying to raise awareness and funds to combat muscular dystrophy in his ...

Dyne Therapeutics (DYN) announced that the European Commission has granted orphan drug designation for DYNE-251 for the treatment of Duchenne ...

The antimalarial drug mefloquine could help treat genetic diseases such as cystic fibrosis, Duchenne muscular dystrophy, as well as some cancers.

Newborn screening is also cost-effective. Testing that takes just a few dollars per baby can save families and the health ...

There are thought to be less than 30 children suitable for the treatment which slows the progress of Duchenne muscular dystrophy (DMD). The condition tragically has a life expectancy is just 26 years.