Biotech firms are engineering smarter, safer gene delivery systems to enhance the safety and efficacy of genetic medicines.

If administered early, gene therapy has the potential to change the medical history of children born with metachromatic ...

Hathway’s technology uses natural epigenetic processes to dial gene activity up or down, rather than rewriting the genetic code. The company is using this to develop therapies for rare diseases and ...

One assay applies to bioprocesses that use the HEK293 human embryonic kidney cell line, often used in gene therapy development.

Hemophilia represents a rare, lifelong bleeding disorder characterized by the blood's inability to clot normally. While management strategies have advanced ...

There are many different conditions that are recognized as mental illnesses. The more common types include: Other diseases or conditions, including various sleep-related problems and many forms of ...

Japanese pharmaceutical company Takeda and domestic biotech company Belief BioMed jointly announced on Thursday that the gene therapy drug Dalnacogene Ponparvovec Injection has received approval ...

In May 2018, North Carolina awarded the Novartis gene therapy division (then called AveXis, later renamed Novartis Gene Therapies) an initial job development investment grant to build a new ...

So says, Gerhard Bauer, ex-director of the UC Davis GMP manufacturing facility and co-author of a new study examining cell and gene therapy production ... operate in. Any process changes require ...

Gene therapy has emerged as a promising frontier in cystic fibrosis research, offering the potential to not just alleviate symptoms, but to address the genetic root of the disease itself. In this ...

Today, a brief rundown of news involving Ferring Pharmaceuticals and Solu Therapeutics, as well as updates from the American Society of Hematology, Bristol Myers Squibb, and PureTech Health that you ...