By John Lauritsen Click here for updates on this story Minnesota (WCCO) — An 8-year-old northern Minnesota boy is one of the first in the country to receive a specific type of gene therapy treatment.

Sarepta Therapeutics said Tuesday that a patient died while taking its closely watched gene therapy for muscular dystrophy, ...

The Minnesota Department of Health tests for over 60 different disorders during a newborn screening, and now, two more ...

A young girl faces an uncertain future after she was diagnosed with an extremely rare and debilitating medical condition which has 'put a timeline on her life'.

"God has blessed us with a rainbow baby," the Counting On alum shared on YouTube in September 2023, when announcing her pregnancy with George. "We're so thankful for the gift of this precious life." ...

The study uncovers the molecular 'rules' driving the arrangement of emerin into nanoclusters and the mechanisms leading to their defective assembly in people with muscular dystrophy. A new ...

However, she was newly pregnant at the time with a baby she now shares with Ken ... was terminally ill and suffering from leukemia, muscular dystrophy and asthma. She also claimed that Gypsy ...

Duchenne muscular dystrophy (DMD) is a relatively common rare disease, affecting about one out of every 3,600 baby boys. This X-linked genetic disease affects the dystrophin protein, a component of ...

He is Rafael, also known as Rafita, a 1-year-and-8-month-old baby from Ensenada who was diagnosed with spinal muscular atrophy type 1 when he was just one month old. The singer livestreamed his visit ...

Soaking up the Aussie sun, the actor, who grew up in Wales, showcased his muscular torso as he went shirtless while wearing a pair of navy shorts. The star is best known for his breakout role ...

Matthew, a 19-year-old with muscular dystrophy and autism, was boarding a school bus outside his East Hanover home on the morning of Feb. 10, 2023. It would be their last moment together.