Both patients werevanti-aquaporin 4 antibody-positive, based on which they were diagnosed with NMOSD. Researchers from Spain presented the cases of 2 patients with very late-onset neuromyelitis optica ...

(L-R) Christina Hartman, Kathryn Alexander, and Lesa Brackbill discuss newborn screening at the 2025 World Orphan Drug Congress USA in Boston, Massachusetts (Photo by Larry Luxner) Newborn screening ...

Scutellarein is a naturally occurring flavonoid compound derived from diverse sources. It shares antioxidant and anti-inflammatory properties with other well-known flavonoids. Scutellarein has been ...

Treatment-related adverse events were more frequent in the nipocalimab group than in the control group; however, they all were mild or moderate in severity. Nipocalimab, a monoclonal antibody with ...

VEXAS syndrome is known to be a mimicker of ANCA-associated vasculitis, making it a challenge to distinguish between the disorders. VEXAS (vacuoles, E1 enzyme, X-linked, autoinflammatory, somatic) ...

Last week, I had the incredible honor of speaking at the World Orphan Drug Conference (WODC), where I was invited to participate in a panel about the role of media as a lifeline in amplifying voices ...

After 2 cycles of gemtuzumab ozogamicin, the patient achieved complete remission with clearance of leukemic and abnormal mast cells. A pediatric patient with refractory systemic mastocytosis (SM) ...

After initial treatment with a KIT inhibitor, hematopoietic stem cell transplantation was successful in resolving the symptoms. A new case has been reported in Pediatric Blood & Cancer of systemic ...

Which of the statements below about the symptoms of myelofibrosis (MF) are correct? Select one of the options for each question, then submit your answers to see how well you scored and how other test ...

Researchers investigated the apparent close relationship between IGG4-RD and AAV and whether they arise from shared pathophysiological pathways. A 60-year-old woman was referred for fever and kidney ...

Genes such as NKG7 and ASCL2 were found to be key drivers of CLL and could inform drug sensitivity profiles. A distinct natural killer (NK) cell subset, termed CLL_NK, is a precursor to effector NK ...

Mycophenolate mofetil may have a role in alleviating liver injury secondary to drugs such as avacopan. An elderly female patient with antineutrophil cytoplasmic antibody (ANCA)-associated vasculitis ...