The Muscular Dystrophy Association (MDA) held its first-ever Clays for a Cure event on Friday, Sept. 20. Check out the photos ...
Biotech reported positive interim data from a mid-stage trial of a treatment for the rare muscle disorder Duchenne muscular ...
Wave Life Sciences Ltd. (NASDAQ:WVE) revealed interim data from the ongoing Phase 2 FORWARD-53 study of WVE-N531 for Duchenne ...
Discover Avidity Biosciences' groundbreaking patent for treating facioscapulohumeral muscular dystrophy (FSHD) using a novel polynucleic acid conjugate targeting the DUX4 gene.
Pratteln, Switzerland, September 24, 2024 – Santhera Pharmaceuticals (SIX: SANN) announces that Swissmedic, the Swiss Agency for Therapeutic Products, has accepted for review the marketing ...
A possible gene therapy approval and a series of major trials readouts set the stage for a busy year of drug development in ...
The Cambridge Professional Fire Fighters’ Association held their annual Muscular Dystrophy Boot Drive on Saturday.
Meet Sehba Shah, Pakistan's inspiring woman chess player who lives with muscular dystrophy yet dreams high above the ...
The FDA has granted Orphan Drug and Rare Pediatric Disease Designations to Somite’s cell replacement therapy for the ...
Neu refix granted orphan disease designation (ODD) & rare pediatric disease designation (RPDD) by US FDA for treatment of ...
Six-year-old Cooper Wood was diagnosed with Duchenne muscular dystrophy earlier this year. When his parents applied for a one ...
If you notice traffic backing up and firefighters out at an intersection on Friday and Saturday, don’t worry — it’s all for a ...