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Rare diseases often go undiagnosed or untreated in parts of Africa. A project seeks to change that
She visited Fann hospital in Dakar, where neurologist Dr. Pedro Rodriguez measured her lung capacity. He suspects Mariama had ...
Dailymotion on MSN2h
My Rare Condition Took My Hair & Teeth | BORN DIFFERENT
OLD who was bullied over her rare genetic condition - that severely affects her appearance - has silenced her critics by ...
Investing4d
Palvella Therapeutics secures new patent for rare skin disease gel
This platform is focused on developing therapies for rare genetic skin diseases, many of which are lifelong conditions. Palvella’s lead product candidate is currently under evaluation in the Phase 3 ...
Investing4d
Palvella Therapeutics secures new patent for rare skin disease gel
This platform is focused on developing therapies for rare genetic skin diseases, many of which are lifelong conditions. Palvella’s lead product candidate is currently under evaluation in the ...
CNN on MSN4d
Eddie Vedder’s quest to help cure a rare disease
A string of 2023 solo concerts in Seattle are the backdrop for the film, which chronicles Vedder’s efforts to raise funds for ...
Yahoo Finance4d
Palvella Therapeutics Granted Additional U.S. Patent for QTORIN™ Rapamycin for the Treatment of Microcystic Lymphatic Malformations
rare genetic skin diseases for which there are no U.S. Food and Drug Administration (FDA)-approved therapies, today announced that the United States Patent and Trademark Office (USPTO) issued ...
The Manila Times4d
Palvella Therapeutics Granted Additional U.S. Patent for QTORIN™ Rapamycin for the Treatment of Microcystic Lymphatic Malformations
QTORIN™ rapamycin has been granted Breakthrough Therapy Designation, Orphan Drug Designation, and Fast Track Designation from the U.S. FDA for the treatment of microcystic LMs. In addition to granted ...
Morningstar4d
Palvella Therapeutics Granted Additional U.S. Patent for QTORIN™ Rapamycin for the Treatment of Microcystic Lymphatic Malformations
Palvella is developing a broad pipeline of product candidates based on its patented QTORIN™ platform, with an initial focus on serious, rare genetic skin diseases, many of which are lifelong in ...