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Asianet Newsable on MSN8d
Abeona Therapeutics’ Gene Therapy Gets FDA Nod For Treating Rare Genetic Skin Disease
ZEVASKYN is expected to be available beginning in the third quarter of 2025 through ZEVASKYN Qualified Treatment Centers, ...
Q&A: Two decades of research lead to treatment for rare, painful skin condition
Patients with severe dystrophic epidermolysis bullosa, or EB, have skin so fragile, the slightest touch can lead to ...
BioWorld9d
Abeona’s rare skin disease gene therapy approved by FDA
Barely a year after the U.S. FDA shackled Abeona Therapeutics Inc.’s cell-based gene therapy with a complete response letter, the agency has approved it for treating a rare and genetic skin disease.
Daily Jang6d
Zevaskyn receives FDA approval for rare, genetic skin disorder
The U.S. Food and Drug Administration has approved Zevaskyn for patients suffering from rare, genetic skin disease recessive ...
First Cell-Based Gene Therapy Approved for Rare Skin Disorder
The US Food and Drug Administration (FDA) has approved the first cell-based gene therapy for a rare genetic skin disorder.
Fierce Pharma8d
Abeona enters commercial gene therapy arena with FDA nod for Zevaskyn to treat rare genetic skin disease
Persistence has paid off for Abeona Therapeutics and its gene therapy for recessive dystrophic epidermolysis bullosa (RDEB).
Investigational gene therapy gives children with rare immune disorder a new lease on life
An investigational gene therapy has successfully restored immune function in all nine children treated with the rare and life ...
ABC News11d
Rare diseases often go undiagnosed or untreated in parts of Africa. A project seeks to change that
Rodriguez is trying to change that by connecting patients with genetic testing and medical support, while gathering key data ...
Newsday11d
Rare diseases often go undiagnosed or untreated in parts of Africa. A project seeks to change that
Fatoumata Sané holds her daughter Aissata, 8, who suffers from a rare genetic disease, at their home in ... a tiny scar on his forehead where broken skin has been stitched back together.
SFGate11d
Rare diseases often go undiagnosed or untreated in parts of Africa. A project seeks to change that
Rodriguez is trying to change that by connecting patients with genetic testing and medical support, while gathering key data from those patients and their families. “Most rare disease data has ...