The symposium took place on 18 th March 2025, as part of the Muscular Dystrophy Association (MDA) Clinical & Scientific ...

New York, April 29, 2025 (GLOBE NEWSWIRE) -- The Muscular Dystrophy Association (MDA) today announced the launch of its nationwide campaign focused on amyotrophic lateral sclerosis (ALS ...

"Eleanor Gehrig's legacy lives on through the Muscular Dystrophy Association's work to care for families and accelerate progress against ALS,” said Donald S. Wood, PhD, President and CEO of MDA. "This ...

The purpose of this report is to re-evaluate such a therapeutic program in muscular dystrophy when the drugs are used singly, in combination and with or without exercise. Objective serial ...

The European Medicines Agency (EMA) has recommended granting a conditional marketing authorisation in the European Union (EU) for Duvyzat (givinostat) as a treatment for Duchenne muscular dystrophy ...

Just a few weeks after Avidity Biosciences made a stir with new data on its experimental therapy for Duchenne muscular dystrophy, the biotech has closed a public offering that raised an impressive ...

Pfizer has axed trials of its domagrozumab antibody for Duchenne muscular dystrophy (DMD), after it failed against efficacy targets. Pfizer has been evaluating domagrozumab under the codename PF ...

Last month, we introduced you to Killian, whose health is declining with Duchenne muscular dystrophy. We watched Killian’s mom, Amanda, struggle to get him into and out of the family van ...

Boston, Massachusetts--(Newsfile Corp. - April 29, 2025) - Tevard Biosciences, Inc., a privately held biotechnology company pioneering tRNA-based therapies to cure a broad range of genetic diseases, ...

Mutations in the dysferlin gene lead to limb girdle muscular dystrophy 2B, Miyoshi myopathy and distal anterior compartment myopathy. A cohort of 36 patients affected by dysferlinopathy is described, ...

The Committee for Medicinal Products for Human Use, an arm of the European Medicines Agency known as CHMP for short, has recommended the approval of Duvyzat (givinostat) as a treatment for people with ...

"We Row for William" raised awareness and support for Duchenne Muscular Dystrophy treatment. 57°F ...