An 8-year-old northern Minnesota boy is one of the first in the country to receive a specific type of gene therapy treatment.

The startup is using CRISPR tools to stop errant expression of a gene linked to facioscapulohumeral muscular dystrophy, a ...

When Lauren Clarke was 14, she was diagnosed with a rare, incurable muscle-weakening disorder. Ten years on, she has become ...

Muscular dystrophy, loss of mobility ... be taken to support better nutrition with this disease. People with DMD face a number of challenges to their nutritional health, including both over ...

Dec. 16, 2024 — A novel drug holds promise for treating Duchenne muscular dystrophy (DMD), a rare genetic disorder that causes severe muscle degeneration. Researchers have discovered that an ...

Columnist Shalom Lim is sad to say goodbye to his caregiver of 18 years, but looks forward to the new chapter of life this ...