scientists have developed a new gene replacement therapy in mice that could lead to more effective treatments in humans. The ...

scientists have developed a new gene replacement therapy in mice that could lead to more effective treatments in humans. The findings were published today in the journal Science Translational ...

The MyPEAK-1 trial investigator Milind Desai said: “TN-201 is the first gene therapy to be tested in HCM patients whose disease is caused by mutations to the MYBPC3 gene. For patients with this ...

Scientists from the Allen Institute and Seattle Children’s Research Institute have announced a breakthrough in the development of gene ... paper, mice treated with the new therapy survived ...

Then they wanted to know if they could selectively incorporate the enhancer elements into an adult mouse using adeno-associated virus, a familiar gene therapy tool for introducing gene sequences into ...

scientists have developed a new gene replacement therapy in mice that could lead to more effective treatments in humans. "People who take drugs for epilepsy often complain that the drugs are very ...